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Phase 1/2 Clinical Trial of Intravitreal 4D-125 AAV Gene Therapy in Patients with Advanced XLRP: Interim Safety & Preliminary Activity

  • Cagri G Besirli, MD, PhD, FASRS
  • Video
  • Published 2021

Related

  • Elamipretide, a Mitochondria-Targeted Drug for the Treatment of Vision Loss

    Scott W. Cousins, MD

    Updates from the Field

    2019

  • Episode 201: AMD Drug Updates with Dr. Allen Ho, including Gene Therapy

    Jayanth Sridhar, MD

    Member Podcasts

    2019

  • Precision Subretinal Delivery for Cell and Gene Therapy

    Allen C Ho, MD FASRS

    Updates from the Field

    2019

Category: Hereditary Retinal Disease & Genetics

  • Gene Therapy
  • inherited retinal disease
  • Adeno-associated virus (AAV)
  • XLRP
  • RPGR

See more

  • Updates from the Field
  • Cagri G Besirli, MD, PhD, FASRS
  • ASRS Multimedia Library
  • Video
  • Audio
  • Images
  • Collections
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